hemophilia

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The FDA Has Just Approved a Drug That Costs $3.5M a Dose

Hemgenix is a one-time treatment for the blood-clotting disorder hemophilia

(Newser) - US health regulators on Tuesday approved the first gene therapy for hemophilia, a $3.5 million one-time treatment for the blood-clotting disorder. The FDA cleared Hemgenix: It's an IV treatment for adults with hemophilia B, the less common form of the genetic disorder, reports the AP . Currently, patients receive...

Anti-Bleeding Drug Could Save Lives in the ER

100,000 trauma patients could benefit

(Newser) - A drug used to slow bleeding during surgery could save the lives of scores of trauma patients if used in emergency rooms, a new study suggests. UK researchers found that the drug tranexamic acid reduced bleeding deaths among trauma patients by a sixth, HealthDay reports. As 600,000 such patients...

Drug Targets Hundreds of Disorders
Drug Targets Hundreds of Disorders

Drug Targets Hundreds of Disorders

Magic bullet hits mutations that prompt 1,800 genetic diseases

(Newser) - A magic bullet that could treat cystic fibrosis, muscular dystrophy, hemophilia and more than 1,800 other genetic disorders could be available by 2009. Lee Sweeney of UPenn, leader of the team developing the drug, tells the Times of London: “It doesn’t just target one mutation that causes...

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