orphan drugs

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This Drug Just Got the FDA's OK—and an $89K Price Tag

Marathon Pharmaceuticals to sell deflazacort for $89K

(Newser) - A drug sold for years overseas to treat a rare form of muscular dystrophy was OKed Thursday by the FDA to be sold in the US, but it comes at a high price. The Wall Street Journal reports the now-FDA-approved deflazacort will be offered by Marathon Pharmaceuticals for $89,000... More »

Jack Klugman's Quiet Legacy: Lifesaving Crusader

Actor shoved Congress to pass Orphan Drug Act of 1982

(Newser) - Most obituaries of Jack Klugman remember him for his roles on The Odd Couple and Quincy, M.E., but the actor had another legacy that few people remember, reports the Washington Post . Klugman was a fierce advocate of the Orphan Drug Act of 1982, a bill that aimed to provide... More »

Pharma Under Fire Over Pricey Drugs for Kids

Lawmakers lash astronomical hikes in drugs for rare diseases

(Newser) - In the face of astronomical hikes in the price of drugs used to treat children, a congressional committee is looking into why companies have increased prescription costs as much as 18-fold when related research and marketing expenses are stable, according to lawmakers. One such company charges $69,000 for a... More »

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